Motor Responses in Pediatric Pompe Disease in the ADVANCE Participant Cohort

Tina Duong, Priya S. Kishnani, Kristina An Haack, Meredith C. Foster, James B. Gibson, Catherine Wilson, Si Houn Hahn, Richard Hillman, David Kronn, Nancy D. Leslie, Loren D.M. Peña, Susan E. Sparks, David W. Stockton, Pranoot Tanpaiboon, John W. Day

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Nursing and Health Professions

Pharmacology, Toxicology and Pharmaceutical Science