Respiratory function during enzyme replacement therapy in late-onset Pompe disease: longitudinal course, prognostic factors, and the impact of time from diagnosis to treatment start

David W. Stockton, Priya Kishnani, Ans van der Ploeg, Juan Llerena, Matthias Boentert, Mark Roberts, Barry J. Byrne, Roberto Araujo, Sonia S. Maruti, Nathan Thibault, Karien Verhulst, Kenneth I. Berger

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Pharmacology, Toxicology and Pharmaceutical Science

Neuroscience

Psychology